Gene therapy for cystic fibrosis
Dr Chantelle McIntyre
The University of Adelaide
From birth, individuals who inherit cystic fibrosis (CF) face a life-long, relentless, regime of medical treatments and physiotherapy in an effort to manage respiratory and digestive complications, and thereby prolong life. However, no cure for CF exists, and premature death is inevitable. Respiratory failure is the most common cause of death. The current study is focused towards developing gene therapy for CF airway disease. This treatment approach has the potential to provide long lasting therapeutic benefit to patients, significantly improving their quality of life, and extending life.